• Perguntas frequentes
  • Glossário
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Perguntas frequentes

Why are some conditions more suitable for gene and cell therapies than others?
There is an approved treatment available for my condition - why can't I receive it?
How to look for approved medicines?
How are medicines developed and approved?

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Glossário

Adeno-associated virus (AAV)
Adenovirus
Adult stem cells
Antibody
Antigen
Base editors
Cas9 nuclease
Chimeric Antigen Receptor (CAR)
Chromosome
Clinical trial

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Potential Gene Therapies for Duchenne Muscular Dystrophy

Related topics:
Muscle and Skeletal Diseases Muscular Dystrophy Gene Editing Gene Therapy Research
Action Duchenne Logo

Action Duchenne have created a page on gene therapy for Duchenne Muscular Dystrophy. Here you will find an explanation of the underlying principles of gene therapy for DMD, and an overview of the different avenues of research being explored.

Action Duchenne: Gene Therapy

Action Duchenne logo

Copyright Action Duchenne - Registered Charity No 1101971 - Scottish Charity No SC043852

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Muscular dystrophy: how could stem cells help?

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Gene Therapy Basics

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Temas relacionados Cell and Gene Fundamentals Gene Editing Gene Therapy
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What is gene and cell therapy?

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Temas relacionados Cell and Gene Fundamentals Cell Therapy Gene Editing Gene Therapy
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