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Why are some conditions more suitable for gene and cell therapies than others?

There is an approved treatment available for my condition - why can't I receive it?

How to look for approved medicines?

How are medicines developed and approved?

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Glossary

Adeno-associated virus (AAV)

Adult stem cells

Chimeric Antigen Receptor (CAR)

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Gene Editing

Gene editing is the process of activating or de-activating a gene, or multiple genes. These factsheets discuss the techniques involved, how it can be used in the lab and clinic, and the ethical implications of these technologies.

Resources & Factsheets

EuroGCT Resource

Cell Basics teaser image

What is gene and cell therapy?

Related Topics Cell and Gene Fundamentals Cell Therapy Gene Editing Gene Therapy

EuroGCT Resource

What conditions can currently be treated using gene and cell therapy?

Related Topics Blood disorders Cancer Eye Disease Immune Conditions Multiple Sclerosis Rare Diseases Blood Stem Cells CAR-T Therapy Cell Therapy Current and Potential Uses Explore Stem Cells Factsheets Gene Editing Gene Therapy

From disease to cure: the story of an outstanding scientific result

Related Topics Immune Conditions Rare Diseases Current and Potential Uses Gene Editing Gene Therapy

Genetics Shambles

Related Topics Cell and Gene Fundamentals Ethics and Society Explore Stem Cells Gene Editing Gene Therapy Research

CAR T-cell therapy phases

Related Topics Blood disorders Cancer CAR-T Therapy Gene Editing Reprogramming

Easy-read information on cystic fibrosis

Related Topics Cystic Fibrosis Cell and Gene Fundamentals Gene Editing Gene Therapy

Cystic Fibrosis Trust: Genetic Therapies Glossary

Related Topics Cystic Fibrosis Cell and Gene Fundamentals Gene Editing Gene Therapy

EuroGCT Resource

EuroGCT stock DNA graphic

Why are some conditions more suitable for gene and cell therapies than others?

Related Topics Cell Therapy Clinical Trials Current and Potential Uses Disease Modelling Ethics and Society Gene Editing Gene Therapy Methods and Tools Patient Involvement Policy & Regulation Research

Screenshot from ASGCT's video 'Gene Therapy Approaches'. Two cartoon figures look at text listing gene therapy techniques: Gene Addition, RNA Therapy, Gene Silencing, Cell Therapy, Gene Editing

Gene Therapy Approaches

Related Topics Cell and Gene Fundamentals Cell Therapy Clinical Trials Current and Potential Uses Gene Editing Gene Therapy Methods and Tools Reprogramming

Potential Gene Therapies for Duchenne Muscular Dystrophy

Related Topics Muscle and Skeletal Diseases Muscular Dystrophy Gene Editing Gene Therapy Research