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FAQs

Why are some conditions more suitable for gene and cell therapies than others?
There is an approved treatment available for my condition - why can't I receive it?
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Glossary

Adeno-associated virus (AAV)
Adenovirus
Adult stem cells
Antibody
Antigen
Base editors
Cas9 nuclease
Chimeric Antigen Receptor (CAR)
Chromosome
Clinical trial

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Resources

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Jonathan's story teaser

Jonathan's story: Stem Cells and Myelin

Related Topics Multiple Sclerosis Neurological Disorders Clinical Trials Research
Dolly and Beyond Teaser image

Dolly and Beyond

Related Topics Embryonic Stem Cells Ethics and Society
Peter's Story Teaser

Peter's Story: stem cells and blood cancers

Related Topics Cancer Blood Stem Cells Clinical Trials Current and Potential Uses Explore Stem Cells Patient Involvement Research
Paula's Story teaser

Paula's story: stem cells and brain repair

Related Topics Neurological Disorders Parkinson's Disease Current and Potential Uses Explore Stem Cells Research
Word-cloud of gene editing terminology

Genome editing and stem cells: questions and answers

Related Topics Current and Potential Uses Ethics and Society Gene Editing Gene Therapy Research
Image of front cover of the white paper "Organoids - from stem cells to future technologies"

Organoids - from stem cells to future technologies

Related Topics Clinical Trials Disease Modelling Methods and Tools
cell culture teaser

Cell Culture

Related Topics Disease Modelling Explore Stem Cells Methods and Tools
Stem Cell Futures teaser

Stem cell futures: An introduction to iPS cells

Related Topics Current and Potential Uses Explore Stem Cells iPS cells Methods and Tools Reprogramming
What is cloning teaser

What is cloning, and what does it have to do with stem cell research?

Related Topics Current and Potential Uses Disease Modelling Ethics and Society Explore Stem Cells Methods and Tools
cell fate teaser

Cell Fate: Journeys to Specialisation

Related Topics Cell and Gene Fundamentals Explore Stem Cells

What conditions can currently be treated using gene and cell therapy? (Full table)

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Key MHRA Resources

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Clinical Development Flowchart

EMA Non-clinical development

Non-clinical Development Flowchart

EMA quality flowchart

Quality Flowchart

EMA teaser

ATMP Overview

EMA infosheet

EMA tools for academic medicine developers

EMA logo

Key European Medicines Agency (EMA) Resources

International Society for Stem Cell Research patient handbook cover

A Closer Look At Stem Cells

Related Topics Clinical Trials Explore Stem Cells Unproven Treatments
EuroGCT Resource
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What is gene and cell therapy?

Related Topics Cell and Gene Fundamentals Cell Therapy Gene Editing Gene Therapy
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