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Why are some conditions more suitable for gene and cell therapies than others?
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Glossary

Adeno-associated virus (AAV)
Adenovirus
Adult stem cells
Antibody
Antigen
Base editors
Cas9 nuclease
Chimeric Antigen Receptor (CAR)
Chromosome
Clinical trial

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Resources

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Gene and cell therapies: an introduction for policy-makers

Gene and cell therapies: an introduction for media professionals

Cartoon graphic of two figures hugging. One wears an insulin patch on their arm.

Connecting young people with Type 1 Diabetes through science

Related Topics Diabetes Cell Therapy Current and Potential Uses Embryonic Stem Cells Patient Involvement Reprogramming Research Stem Cell News
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Case Studies

Do you have to make a decision concerning the treatment of someone under your professional care?

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Identifying Genetic Disease

Related Topics Current and Potential Uses Ethics and Society Methods and Tools
Screenshot from ASGCT's video 'Gene Therapy Approaches'. Two cartoon figures look at text listing gene therapy techniques: Gene Addition, RNA Therapy, Gene Silencing, Cell Therapy, Gene Editing

Gene Therapy Approaches

Related Topics Cell and Gene Fundamentals Cell Therapy Clinical Trials Current and Potential Uses Gene Editing Gene Therapy Methods and Tools Reprogramming
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Alcyomics and NA-ATTC Current Guidelines on Advanced Cell Therapy Pre-Clinical Procedures

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The Li lab: Organoids (Video)

Related Topics Bowel Disease Organoids Tissue Engineering
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The Jensen Group: Our Cellular Fortress (Animation)

EuroGCT Resource
EuroGCT

Case Study: Strimvelis

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Creating EU market access roadmaps for cell and gene therapies

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EFPIA Challenges and facilitators in the development of orphan and paediatric medicines

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EFPIA Intellectual Property

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EFPIA About medicines

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EFPIA Value of medicines

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EFPIA The root cause of unavailability and delay to innovative medicines

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EFPIA Back Innovation, Boost Access

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EPFIA Shifting the paradigm for ATMPs

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The European Federation of Pharmaceutical Industries and Associations (EFPIA) Resources

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