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Why are some conditions more suitable for gene and cell therapies than others?

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Glossary

Adeno-associated virus (AAV)

Adult stem cells

Chimeric Antigen Receptor (CAR)

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Gene Therapy

Gene therapy is an important tool in treating genetic conditions, allowing a faulty gene to be corrected or replaced. In these factsheets and resources, you can learn about the tools and techniques used in gene therapy, and how they can be used to better understand and to treat illness.

Resources & Factsheets

EuroGCT Resource

EuroGCT stock DNA graphic

Why are some conditions more suitable for gene and cell therapies than others?

Related Topics Cell Therapy Clinical Trials Current and Potential Uses Disease Modelling Ethics and Society Gene Editing Gene Therapy Methods and Tools Patient Involvement Policy & Regulation Research

English

EuroGCT Resource

Laboratory-grown nerve cells, shown with fluorescent green dye against a black background

Parkinson's Disease: How could gene and cell therapy help?

Related Topics Neurological Disorders Parkinson's Disease Cell Therapy Clinical Trials Current and Potential Uses Factsheets Gene Therapy iPS cells Reprogramming

Compassionate use

Related Topics Rare Diseases Cell Therapy Clinical Trials Current and Potential Uses Gene Therapy Patient Involvement Policy & Regulation Unproven Treatments

Screenshot from ASGCT's video 'Gene Therapy Approaches'. Two cartoon figures look at text listing gene therapy techniques: Gene Addition, RNA Therapy, Gene Silencing, Cell Therapy, Gene Editing

Gene Therapy Approaches

Related Topics Cell and Gene Fundamentals Cell Therapy Clinical Trials Current and Potential Uses Gene Editing Gene Therapy Methods and Tools Reprogramming

Potential Gene Therapies for Duchenne Muscular Dystrophy

Related Topics Muscle and Skeletal Diseases Muscular Dystrophy Gene Editing Gene Therapy Research

Word-cloud of gene editing terminology

Genome editing and stem cells: questions and answers

Related Topics Current and Potential Uses Ethics and Society Gene Editing Gene Therapy Research

EuroGCT Resource

DNA teaser image

CAR-T Therapy

Related Topics Blood disorders Cancer Immune Conditions Rare Diseases Blood Stem Cells CAR-T Therapy Cell Therapy Clinical Trials Current and Potential Uses Factsheets Gene Editing Gene Therapy

Cartoon showing a person looking at the contents of a cell

Gene Therapy Basics

Related Topics Cell and Gene Fundamentals Gene Editing Gene Therapy

Cartoon depicting different kinds of viral vectors (clockwise from bottom left: lentiviral, adenoviral, retroviral, adeno-associated viral)

Vectors 101

Related Topics Cell Therapy Disease Modelling Gene Editing Gene Therapy Methods and Tools Reprogramming