Ex vivo gene therapy involves the collection of cells from an individual patient, followed by modifications (insertion, deletion or correction) of the disease-causing gene (called the gene of interest) in a laboratory, and finally, reintroduction of the modified cells back into the patient to treat a specific disorder. This approach allows for controlled treatment and selection of cells that are reintroduced back into the patient.
This entry was provided by the doctoral students of the GetRADI collaborative network. GetRADI is funded by the European Union. Views and opinions expressed are however those of the author(s) only and do not necessarily reflect those of the European Union or the European Research Executive Agency. Neither the European Union nor the granting authority can be held responsible for them.